New FDA Plausible Mechanism Framework Spurs Development of Personalized In Vivo Prime Editing Platform for Urea Cycle Disorders

Researchers from Children's Hospital of Philadelphia (CHOP) and Penn Medicine, along with collaborating institutions, ...

The $578 Billion Regenerative Medicine Market Has a Manufacturing Problem. One Company Just Solved the First Step

The FDA has approved more than 40 cell and gene therapy products. The regenerative medicine market is projected to reach $578 ...
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CRISPR: A gene-editing superpower

Any molecular biologist will tell you that genetic engineering is tricky. But up until recently we might be witnessing a new ...

Down syndrome study suggests early RNA editing shifts may reshape fetal brain circuits

A collaborative research study co-led by scientists at the Icahn School of Medicine at Mount Sinai and the Liber Institute ...
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Excessive RNA editing enzyme alters brain circuit formation in Down syndrome

A collaborative research study co-led by scientists at the Icahn School of Medicine at Mount Sinai and the Liber Institute for Brain Development has for the first time identified a biological process ...